Background: Tepotinib, an oral MET TKI, showed robust and durable efficacy and safety of tepotinib in patients with ≥3 years follow-up in the VISION study. Here, we report long-term efficacy of tepotinib in clinically relevant subgroups of patients with ≥3 years follow-up (data cut-off: May 20, 2024).
Methods: Patients with advanced/metastatic METex14 skipping NSCLC, detected by tissue (T+) and/or liquid biopsy (L+), received tepotinib 500 mg (450 mg active moiety) QD. Primary endpoint was objective response (RECIST v1.1) by IRC. Subgroup analyses were preplanned; exploratory analysis of brain lesions was conducted using RANO-BM criteria.
Results: Of 313 patients (median age 72.0 years), 41.2% were ≥75 years, 47.6% had smoking history, and 18.2% had brain metastases at baseline; 208 patients were T+ (first line [1L]: 111; second-or-later line [2L+]: 97), 178 were L+ (1L: 95; 2L+: 83), and 73 patients were T+/L+.
T+ patients had an ORR of 54.8% (mDOR, 17.4 months) while L+ patients had an ORR of 51.7% (mDOR, 15.2 months). L+ patients had shorter time-dependent endpoints, potentially due to a higher baseline disease burden.
In patients aged <75 years (n=184), ORR was 55.4% (mDOR, 19.4 months) versus 46.5% (mDOR, 15.7 months) in patients ≥75 years (n=129). Patients with smoking history (n=149) had an ORR of 56.4% (mDOR, 18.0 months), versus 47.4% (mDOR, 20.8 months) in patients without (n=154).
Among 57 patients with baseline brain metastases, systemic ORR was 56.1% (mDOR, 9.0 months), versus 50.8% (mDOR, 19.4 months) in patients without (n=256). In patients with brain tumors as target lesions evaluable by RANO-BM (n=15), intracranial ORR was 66.7% (DCR, 86.7%).
Conclusions: Tepotinib continued to show robust and durable efficacy in patients with ≥3 years follow-up, irrespective of T+/L+ status, age, smoking status, or brain metastases at baseline, consistent with previously reported findings of overall population.